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Increasing interest in gene therapy as a novel approach to treat a number of diverse inherited diseases and is driving expectation that this line of research will continue to thrive in future years. Finally, after decades of work, researchers are seeing payoff in the form of market-released gene therapies that are bringing new hope to patients who previously had limited therapeutic options. For neurology, a specialty with a significant percentage of diseases with a genetic origin, gene therapy is particularly promising as a breakthrough treatment.